Ongoing projects

Rare Partners established collaborations with several scientists with the final scope of transforming important research results into development projects, which ultimately could provide new therapies and diagnostic tools to patients suffering from rare diseases.

Sirolimus in Sickle Cell Disease disease Sickle Cell Disease (SCD)

Development of a therapy for Usher Syndrome disease Sindrome di Usher

Sirolimus in beta-thalassemia disease Beta-thalassemia

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